Gene therapy can treat AHDS

A team of international scientists, led by Dr. Gad Vatine of Ben Gurion University, discovered a thyroid hormone MCT8 mutation causes Allan-Herndon-Dudley syndrome (AHDS). Sufferers cannot walk or talk. They developed a gene therapy AAV9-MCT8 to restore the hormone’s function.

https://in.bgu.ac.il/en/pages/news/AHDS_neurology.aspx

https://www.liebertpub.com/doi/10.1089/thy.2022.0034

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